orphan drug
"Orphan drugs" are crucial for treating rare diseases, often receiving special incentives to encourage their development.
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Definition
C1Medicine
(technical, regulatory)A pharmaceutical product developed to treat rare medical conditions that affect a small population.
Example
- The company received incentives to develop an orphan drug for a rare genetic disorder.
C1Regulatory
(US, law)A drug intended to treat a disease affecting fewer than 200,000 people in the United States.
C1Regulatory
(EU, law)A drug aimed at diagnosing, preventing, or treating a life-threatening or chronically debilitating condition affecting not more than 5 in 10,000 people in the European Union.
C1Regulatory
(Japan, law)A drug designed for conditions affecting fewer than 50,000 patients in Japan, often with high medical need.
Similar
Terms that have similar or relatively close meanings to "orphan drug":